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Neschadim et al., 2007 - Google Patents

A roadmap to safe, efficient, and stable lentivirus-mediated gene therapy with hematopoietic cell transplantation

Neschadim et al., 2007

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Document ID
8859327228267746711
Author
Neschadim A
McCart J
Keating A
Medin J
Publication year
Publication venue
Biology of Blood and Marrow Transplantation

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Hematopoietic stem cells comprise a prominent target for gene therapy aimed at treating various genetic and acquired disorders. A number of limitations associated with hematopoietic cell transplantation can be circumvented by the use of cells stably modified by …
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