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Samulski, 1994 - Google Patents

ADENO-ASSOCIATED VIRUS-BASED VECTORS FOR HUMAN

Samulski, 1994

Document ID
3011535289605438919
Author
Samulski R
Publication year
Publication venue
Gene Therapy: From Laboratory to the Clinic

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Snippet

The concept of gene therapy is simple: a form of molecular surgery by which one replaces a defective gene with an identifiable characterized normal counterpart. The end results of such a practice are correction of the defective gene and rescue of the phenotype (Fig. 11.1). While …
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